Inherited Eye Disorders

Clinical trials for inherited retinal disorders like Leber congenital amaurosis (LCA) have demonstrated that CRISPR gene editing can safely improve vision in a significant number of participants.

Sources

• CRISPR Gene Editing Leads to Improvements in Vision for People With Inherited Bl
• Gene Editing Improves Vision in Some People With Inherited Blindness
• Participants of pioneering CRISPR gene editing trial see vision improve - OHSU N
• oculargenomics.meei.harvard.edu
• Two CHOP Patients with an Inherited Blindness Successfully Treated with Gene Edi

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